Pompe disease

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Biotech

Bayer ditches 1 AAV gene therapy from Pompe disease pair

Bayer has discontinued a phase 1-stage gene therapy for a rare disorder in favor of a similar candidate.
James Waldron Mar 4, 2026 9:59am
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Denali ph. 1 Pompe plans hit with clinical hold

Dec 4, 2025 11:52am
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Roche pumps brakes in Pompe after assessing competition

Jul 25, 2024 6:32am
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Crosswalk grabs compounds from abandoned Takeda, Codexis collab

Jul 2, 2024 9:55am
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After FTC stalled Sanofi deal, Shionogi bags Maze's Pompe drug

May 10, 2024 5:02am
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Sanofi CEO does not rule out future Pompe BD despite FTC moves

Jan 10, 2024 3:37pm