orphan drug

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Biotech

Small molecules are 'resurgent' in orphan drug R&D: Evaluate

Small molecules make up almost half of the 20 most valuable orphan drugs in development across biopharma, according to an Evaluate analysis.

James Waldron Mar 12, 2026 10:30am

RNA Concept 3D Render

RNA biotech emerges with $52M and clinical rare disease asset

Aug 25, 2025 10:13am

Congress senate house government US

Fierce Pharma

Senate revives Orphan Cures Act in Trump's tax bill

Jun 30, 2025 10:09am

Combine

More collaborative FDA can accelerate rare disease R&D: report

Sep 13, 2024 5:00am

pipeline pipes RD research

As pharma eyes shiny obesity drugs, Vertex tops orphan drug list

Apr 24, 2024 12:01am

Pfizer

Pfizer punts pair of orphan drugs amid rare disease R&D rethink

Jan 31, 2023 9:15am