muscular dystrophy

Metallic arrow symbols illuminated by blue and magenta lights forming a graph on blue and magenta background
Biotech

BridgeBio's muscle weakness data impress ahead of FDA filing

BridgeBio took another step toward the approval of its muscle weakness candidate, reporting phase 3 efficacy data that analysts called impressive.
Nick Paul Taylor Mar 12, 2026 10:30am
Stop sign

PepGen hit with partial hold, analyst blames 'understaffed FDA'

Mar 5, 2026 5:45am
Sarepta Sarepta Therapeutics

Sarepta faces new scrutiny after 3rd patient death

Jul 18, 2025 10:19am
Bones doctor

Edgewise drug lowers biomarker in ph. 2 muscular dystrophy trial

Dec 16, 2024 7:40am
Needle sewing thread and fabric

DMD gene therapy uses cells to stitch together mRNA in mice

Nov 14, 2024 3:10pm
wheelchair

Avidity therapy shows possible benefit in muscular dystrophy

Jun 12, 2024 7:00am