mucopolysaccharidosis type I or Hurler syndrome

MPS Families Carry Coffin to FDA
Biotech

Rare disease advocates stage 'funeral' at FDA, make 4 demands

More than 100 marchers carried a coffin to the FDA in a symbolic protest highlighting lives they say could be lost to regulatory delays.
Gabrielle Masson Mar 18, 2026 5:25pm
Blood brain barrier

Trial shows ArmaGen drug improves cognition in Hurler patients

Feb 17, 2017 8:02am