Huntington’s disease

Senior FDA official fires back at uniQure amid controversy

A senior FDA official said the agency never agreed with uniQure's plan, saying “the FDA will always say, ‘Well, we have to see the data when we get it.’”

Angus Liu , Darren Incorvaia Mar 5, 2026 3:33pm

UniQure, FDA back-and-forth intensifies

Mar 5, 2026 11:55am

FDA demands ph. 3 trial of uniQure's Huntington's gene therapy

Mar 2, 2026 10:45am

uniQure's gene therapy for Huntington's hits FDA roadblock

Nov 3, 2025 10:03am

Ferrer nabs European rights for ALS asset in €500M pact

Apr 28, 2025 2:40pm

A close-up of a mouse that appears to be in the process of being digitized created by AI

Gene therapy lowers toxic protein in mice with Huntington's

Feb 28, 2025 1:01pm