Hunter syndrome

MPS Families Carry Coffin to FDA

Biotech

Rare disease advocates stage 'funeral' at FDA, make 4 demands

More than 100 marchers carried a coffin to the FDA in a symbolic protest highlighting lives they say could be lost to regulatory delays.

Gabrielle Masson Mar 18, 2026 5:25pm

stack of letters mail envelopes

FDA details Regenxbio rare disease rejection

Mar 3, 2026 12:56pm

Image of a neon sign with the word no lit up next to an unlit yes

FDA rejects Regenxbio's Hunter syndrome gene therapy

Feb 9, 2026 4:05pm

king crown queen royalty monarchy gold winner top

Royalty's $275M financing deal for Denali drug awaiting FDA nod

Dec 4, 2025 10:20am

Clock in front of the subway

Denali's Hunter syndrome drug latest to be hit by FDA delay

Oct 14, 2025 8:09am

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Regenxbio's Hunter gene therapy latest to face FDA delay

Aug 19, 2025 10:30am