genetic diseases

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Series B round of $125M will fund Diagonal's move into clinic

With a $125 million series B financing round, Diagonal Therapeutics has made a vertical move to advance its first-in-class rare disease drug, DIAG723.

Kevin Dunleavy Jan 8, 2026 6:30am

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After $4.8B Amicus buy, BioMarin drops genetic disease asset

Dec 22, 2025 11:12am

Ipsen fails to land pivotal rare disease trial

Dec 19, 2025 3:37pm

Denali ph. 1 Pompe plans hit with clinical hold

Dec 4, 2025 11:52am

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Pharvaris clocks a pivotal win in race for rapid HAE relief

Dec 3, 2025 9:10am

Genetic medicines biotech halves team

Nov 20, 2025 10:15am