gene therapy

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Biotech

Regenxbio gene therapy passes interim test as pivotal data loom

Regenxbio has guided its DMD gene therapy candidate through another test, reporting a clean safety profile and functional improvements.
Nick Paul Taylor Mar 12, 2026 5:49am
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Senior FDA official fires back at uniQure amid controversy

Mar 5, 2026 3:33pm
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UniQure, FDA back-and-forth intensifies

Mar 5, 2026 11:55am
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Bayer ditches 1 AAV gene therapy from Pompe disease pair

Mar 4, 2026 9:59am
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FDA demands ph. 3 trial of uniQure's Huntington's gene therapy

Mar 2, 2026 10:45am
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Sarepta CEO to retire, citing 'shocking and ironic twist of fate'

Feb 26, 2026 11:30am