gene therapy

Fabry disease
Biotech

Cash-strapped Sangamo seeks partner for new gene therapy

Sangamo Therapeutics’ investigational gene therapy appears to improve kidney function at 52 weeks for patients with a rare genetic disorder.
Gabrielle Masson Jun 24, 2025 11:53am
Reorganization team change restructure

Industry disappointed as FDA reportedly puts Verdun on leave

Jun 20, 2025 1:53am
Redbrick building with Sarepta name and logo
Favicon Fierce Pharma

2nd patient dies after Sarepta's DMD gene therapy Elevidys

Jun 16, 2025 10:58am
An artists depiction of DNA molecules made up of tiny particles

RegenXBio links DMD gene therapy to improved outcomes

Jun 5, 2025 8:52am
Make a delay and accumulation of outstanding tasks Full stop

Rocket crashes as gene therapy patient dies, FDA imposes hold

May 27, 2025 9:49am
a lot of scissors

Gene editor shelves sole clinical asset, lays off 25% of staff

May 19, 2025 2:28pm